Below is a listing of treatments and therapies for PNH. Click on one to read more information or connect with others currently using it.
Overview
A bone marrow transplant is currently the only cure for paroxysmal nocturnal globunaria (PNH). When someone with PNH develops severe complications such as bone marrow failure, severe aplastic anemia, or… read more
Overview
Depending on several factors, you may be eligible to participate in clinical trials studying new treatments for paroxysmal nocturnal hemoglobinuria (PNH). Clinical trials are the only way that new treatments… read more
Overview
Fabhalta is a prescription drug approved by the U.S. Food and Drug Administration (FDA) to treat adults with paroxysmal nocturnal hemoglobinuria (PNH). Fabhalta is also known by its drug name, iptacopan.… read more